Corcept Therapeutics laboratory equipment used in advanced biomedical research

INNOVATION

1 May 2026

The Gene Fix That's Rewriting a Death Sentence for Kids

FDA approves Kresladi, a one-time gene therapy for LAD-I, a rare immune disorder that once left children with few options and little hope

GENA by Sivotec exhibition stand with three delegates meeting

TECHNOLOGY

29 Apr 2026

Ten Seconds to an Answer Years in the Making

A Florida startup's AI platform cuts rare genetic disease diagnosis from days to seconds and it's already been used in 162,000 cases acros...

Regeneron Pharmaceuticals corporate office building exterior

REGULATORY

23 Apr 2026

Breaking the Quiet With a Landmark Genetic Milestone

FDA approves Otarmeni, a groundbreaking gene therapy from Regeneron that restores natural hearing to children with rare genetic mutations

Lab technician in blue glove inserting a sample vial into branded clinical storage trays

PARTNERSHIPS

21 Apr 2026

Curing the Rare Disease Data Crisis

Lunai Bioworks and Geneial join forces to transform fragmented patient records into structured assets, accelerating cures for rare disorde...

Lab scientist with safety goggles using microscope in research lab

MARKET TRENDS

16 Apr 2026

The Billion-Dollar Race to Cure the Rare

Orphan drug markets are projected to surpass $243 billion this year as genetic testing and precision medicine transform the biotech landsc...

Darzalex injection boxes displayed on pharmacy shelf

MARKET TRENDS

2 Apr 2026

Curing the Few, Billing the Many

Rare disease therapies are on track to top $400B in global sales by 2032, buoyed by policy tailwinds and a blockbuster pipeline

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